TREAT-NMD

TREAT-NMD
Translational Research in Europe - Assessment and Treatment of Neuromuscular diseases
KeywordsNeuromuscular diseases, clinical research
Project typeNetwork of Excellence
Funding agencyEuropean Commission
ReferenceFP6-036825
ObjectiveImproving trial-readiness worldwide, advancing patient diagnosis and care and accelerating pre-clinical research
Project coordinatorInstitute of Genetic Medicine, Newcastle University
ParticipantsUniversities, pharmaceutical companies, patient organisations
Websitewww.treat-nmd.org

TREAT-NMD (Translational Research in Europe, Assessment and Treatment for NeuroMuscular Disorders) is a global academic network that focuses on advancing research in neuromuscular disorders. It was established in 2007 with its coordination centre at the Newcastle University. As of 2018, the network comprises over a hundred research centres and patient organisations from 54 countries as well as independent academics and patient representatives. The network's aim is to provide infrastructure to accelerating research through supporting collaboration between its members. Its main goals include improving trial-readiness worldwide, advancing patient diagnosis and care and accelerating pre-clinical research.

Through patient registries, TREAT-NMD provides genotype–phenotype correlation between genetic mutations and neuromuscular disease burden.

References

  1. ↑ Leary, Rebecca; Oyewole, Anne; Bushby, Katharine; Aartsma-Rus, Annemieke (6 July 2017). "Translational Research in Europe for the Assessment and Treatment for Neuromuscular Disorders (TREAT-NMD)". Neuropediatrics. 48 (4): 211–220. doi:10.1055/s-0037-1604110. PMID 28683502. S2CID 19283049.
  2. ↑ Bushby, Katharine; Lynn, Stephen; Straub, Volker (July 2009). "Collaborating to bring new therapies to the patient--the TREAT-NMD model". Acta Myologica. 28 (1): 12–5. PMC 2859629. PMID 19772190.
  3. ↑ "TREAT-NMD Alliance Members – Organizations". TREAT Neuromuscular Network. Retrieved 13 June 2018.
  4. ↑ "TREAT-NMD Alliance Members – Individuals". TREAT Neuromuscular Network. Retrieved 13 June 2018.
  5. ↑ "TREAT-NMD : About the TREAT-NMD network". TREAT Neuromuscular Network.
  6. ↑ Willmann, Raffaella; Rüegg, Markus A.; Fairclough, Rebecca J.; Davies, Kay E; Possekel, Stefanie; Meier, Thomas (October 2008). "T.P.3.03 TREAT-NMD-Activity 7: Accelerate preclinical phase of new therapeutic treatment development". Neuromuscular Disorders (Conference abstract). 18 (9–10): 794. doi:10.1016/j.nmd.2008.06.242. S2CID 54330245.
  7. ↑ Mercuri, Eugenio Maria; Mayhew, Anna G; Muntoni, Francesco; Straub, Volker; Van Ommen, Gert-Jan; Voit, Thomas; Bertini, Enrico; Bushby, Katherine (November 2008). "Towards harmonisation of outcome measures for DMD and SMA within TREAT-NMD; report of three expert workshops: TREAT-NMD/ENMC workshop on outcome measures, 12th--13th May 2007, Naarden, The Netherlands; TREAT-NMD workshop on outcome measures in experimental trials for DMD, 30th June--1st July 2007, Naarden, The Netherlands; conjoint Institute of Myology TREAT-NMD meeting on physical activity monitoring in neuromuscular disorders, 11th July 2007, Paris, France". Neuromuscular Disorders (Workshop report). 18 (11): 894–903. doi:10.1016/j.nmd.2008.07.003. PMID 18818076.
  8. ↑ Thompson R, Robertson A, Lochmüller H (2017). "Natural History, Trial Readiness and Gene Discovery: Advances in Patient Registries for Neuromuscular Disease". Rare Diseases Epidemiology: Update and Overview. Advances in Experimental Medicine and Biology. Vol. 1031. pp. 97–124. doi:10.1007/978-3-319-67144-4_5. ISBN 978-3-319-67142-0. PMID 29214567.

Further reading